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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
1-2-1 Meetings/Networking Break
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Peptide CMC & Process Development
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Peptide CMC & Process Development
Integrating peptide ligands into AAV capsids to enhance targeted delivery and cellular uptake, incre
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Peptide CMC & Process Development
Stem cells used in novel cell therapies for respiratory, orthopedic, and wound healing indications n
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Innovation in Therapeutic Modalities
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Innovation in Therapeutic Modalities
How can we effectively integrate the design of oligonucleotides, small molecules, and conjugates int
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Oligonucleotide CMC & Process Development
GRN‑1 leverages a lipid nanoparticle delivery system to deliver mRNA therapeutics targeting metaboli
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Afternoon Refreshments
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
1-2-1 Meetings/Networking Break
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Evening Drinks Reception
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Oligonucleotide CMC & Process Development
Examine regulatory expectations and case studies on toxicity pathways specific to oligonucleotides a
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Innovation in Therapeutic Modalities
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Innovation in Therapeutic Modalities
The therapeutic potential of nucleic acids is expanding rapidly, but their rational design remains a
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Strategic application of advanced analytical techniques can help improve selection of candidates and
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
1-2-1 Meetings/Networking Break
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Oligonucleotides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
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Drug Delivery
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Networking Lunch
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Oligonucleotide CMC & Process Development
Oligo chemical synthesis Downstream processing/purification Analytic development and specifications
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Morning Refreshments
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
1-2-1 Meetings/Networking Break
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Oligonucleotides CMC
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Peptides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
1-2-1 Meetings/Networking Break
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Oligonucleotides CMC
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Innovation in Therapeutic Modalities
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Translational & Clinical Strategy
Registration
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Translational & Clinical Strategy
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Translational & Clinical Strategy
Explore the latest advancements in oligo-based therapeutics including ASOs, siRNA, gRNA, miRNA, apta
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Innovation in Therapeutic Modalities
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Innovation in Therapeutic Modalities
Overcoming Challenges in eccDNA Detection and Direct Isolation Decoding the Biological Role of Circu
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Oligonucleotide CMC & Process Development
Manufacturing of long RNA oligos: Synthesis and analytical strategies and challenges Scaling Up Oli
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