Approaches to Natural history studies and real world data to inform endpoint selection
24 Jun 2024
Salon C
Clinical Studies
- What are the current challenges of analyzing NHS data and or real-world data to inform clinical assessment endpoints without designing bespoke endpoints for rare or even common neurological disease?
- What data tools do you think will be useful/ impactful to ensure clear understanding of disease progression on a clinical scale and enable efficient and useful endpoint design?
- What is the current role for ML/AI generated real world data summarizing the disease condition and endpoint design?
- Are there alternatives to prospectively designed natural history studies to benchmark disease trajectory for clinical scale assessment endpoints?
