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Approaches to Natural history studies and real world data to inform endpoint selection

24 Jun 2024
Salon C
Clinical Studies
  • What are the current challenges of analyzing NHS data and or real-world data to inform clinical assessment endpoints without designing bespoke endpoints for rare or even common neurological disease?
  • What data tools do you think will be useful/ impactful to ensure clear understanding of disease progression on a clinical scale and enable efficient and useful endpoint design?
  • What is the current role for ML/AI generated real world data summarizing the disease condition and endpoint design?
  • Are there alternatives to prospectively designed natural history studies to benchmark disease trajectory for clinical scale assessment endpoints?
Industry Expert
Aneeta Saxena, Medical Director (Epilepsy and Neurodevelopment) - Biogen