Dose Less, Do More: Redefining Specificity in Gene Therapy
18 Sep 2025
Next Gen Vector Engineering & Delivery
- Optimizing tissue tropism, transduction efficiency, and cell-type specificity to lower dosing requirements and enhance safety profiles.
- Addressing pre-existing immunity and enabling effective redosing to broaden long-term therapeutic impact.
- Engineering vectors tailored to new disease contexts—from rare monogenic disorders to solid tumors and complex cell targets.