Designing innovative preclinical data packages to inform the need for long-term follow-up in gene therapy trials and the possibility of delayed adverse events
15 Apr 2025
Gene Therapy Development
- How do we alter/construct preclinical data packages to assess the risk of delayed adverse events and the need for long term follow-up?
- Understanding the risk of delayed adverse events for integrating and gene-editing based therapies in novel products
- Innovations in assay development to better understand PK/PD, persistence, and the impact of long term modification of cells with in vivo gene therapy
Industry Expert
