Advancing AAV Gene Replacement & Editing: Precision Engineering for Durable and Targeted Therapeutic Outcomes
24 Jun 2025
Gene Therapy Manufacturing
- Evaluating the benefits and limitations of different approaches for various genetic disorders
- Optimizing AAV vector design to enhance delivery efficiency, specificity, and durability for improved therapeutic outcomes
- Overcoming immunogenicity and safety concerns to asses immune responses, toxicity risks, and long term patient safety
